Able to provide written informed consent.
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be able to understand and provide written informed consent
Able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be of appropriate mental capacities with sufficient social support so as to be able to complete required study activities (i.e. diet record, etc) and able to provide written informed consent
Patients must be able to understand and provide written informed consent
ARM I&II: Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent.
Patients are able to understand and provide written informed consent prior to trial participation
Able to provide written informed consent
Must be able to provide written informed consent before any screening procedures.
Able to provide written informed consent for the trial
Able to provide written informed consent.
Able to provide written informed consent
Subjects must be able to provide written informed consent.
Patient able to provide written informed consent; parent or guardian of minor patient able to provide written informed consent
Patient able to provide written informed consent for the long-term follow-up gene therapy study: -; parent or guardian of minor patient able to provide written informed consent for the long-term follow-up gene therapy study: -
Patients must be able to comprehend and provide written informed consent
Able to provide written informed consent
Patients must be able to provide written informed consent
Subjects must be able to provide written informed consent
Able to provide written informed consent
Patient must be able to provide written informed consent
Patients must be able to provide written-informed consent
Participant must be able to provide written Informed Consent
Patients are not able to provide written informed consent to study participation
Able to provide written informed consent
Able to provide signed, written informed consent
Patient able to provide written informed consent.
Patient able to provide written informed consent for the long-term follow-up (LTFU) gene therapy study.
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Able to provide written informed consent
Able to provide written informed consent and to follow protocol requirements.
Able to provide informed written consent
Subject is able to provide written informed consent.
Able to provide informed written consent
Patients must be able to provide written informed consent
Able to provide written informed consent
Subjects must be able to give written consent to the study
Able to provide written consent
Able to provide written, informed consent
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Able to provide written informed consent.
Able to provide written informed consent and to follow protocol requirements
Subject is able to voluntarily provide written informed consent.
Patients must be able to provide written informed consent
Able to provide written informed consent
Able to understand and provide written informed consent
Able to understand and provide written informed consent
Able to provide written informed consent, and agree to practicing  forms of birth control during the study
Be able to provide written informed consent
Able to read either English or Spanish and able to provide written (via paper), verbal consent or on-line informed consent
Able to provide written informed consent
Able to provide written informed consent
Patients must be able to provide written informed consent
Be able to provide written informed consent
Able to provide written informed consent
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Able to provide written consent
Able to provide written consent
Patient is able to provide written informed consent prior to study registration
Patients must be able to provide written informed consent
Patients must be able to provide written informed consent
Able to provide written informed consent
Able to provide written consent
Able to provide written consent
Subject and/or guardian is able to provide written informed consent prior to study registration
Patient and/or guardian is able to provide written informed consent prior to study registration
Patient and/or guardian is able to provide written informed consent prior to study registration
Patient and/or guardian is able to provide written informed consent prior to study registration
Able to provide written informed consent
Patients must be able to provide written informed consent
Able to provide written informed consent.
Able to provide written consent
Able to provide written informed consent
Patients must be able to provide written informed consent
Patient and/or guardian is able to provide written informed consent prior to study registration
Subjects must to able to provide informed written consent prior to study entry
Patients must be able to provide written informed consent
Must be able to provide a written informed consent
Able to provide written informed consent
Participants who are not able to understand or provide written informed consent
Able to provide written informed consent.
Able to provide written informed consent